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Alternate Names: Branaplamum
CAS No: 1562338-42-4
PubChem CID: 135565042
Mol Formula: C22H27N5O2
Mol Weight: 393.5 g/mol
IUPAC Name: 5-(1H-pyrazol-4-yl)-2-[6-(2,2,6,6-tetramethylpiperidin-4-yl)oxypyridazin-3-yl]phenol
Commercial / Development Status: Discontinued APIs
Source / Manufacturing Origin: Synthetic APIs
API Description: Branaplam is under investigation in clinical trial NCT02268552 (An Open Label Study of LMI070 (Branaplam) in Type 1 Spinal Muscular Atrophy (SMA)).
